TY  - ADVS
AU  - Davidson,Beverly L.
TI  - RNAi for neurological diseases
T2  - Gene transfer and gene therapy,
PY  - 2014///
CY  - London
PB  - Henry Stewart Talks
KW  - Gene therapy
KW  - Genetic vectors
KW  - Therapeutic use
KW  - Huntington's disease
KW  - Nervous system
KW  - Diseases
KW  - Genetic aspects
KW  - Small interfering RNA
KW  - Gene Transfer Techniques
KW  - Genetic Therapy
KW  - methods
KW  - Genetic Vectors
KW  - therapeutic use
KW  - Huntington Disease
KW  - therapy
KW  - MicroRNAs
KW  - Nervous System Diseases
KW  - RNA Interference
KW  - RNA, Small Interfering
N1  - Animated audio-visual presentation with synchronized narration; Title from title frames; Contents: Repeat expansion diseases -- Polyglutamine (polyQ) repeat diseases -- Huntington's disease -- Vectors for delivering genetic material to brain -- AAVs for delivering RNAi for reducing gene expression -- Artificial miRNAs -- Testing miHD for efficacy -- Off-target silencing -- MRI-guided delivery of AAV into primates -- HTT suppression -- Other gain-of function diseases -- Targeted infusion for broad coverage -- Silencing ataxin-1 -- Nonallele specific silencing: experimental design -- Expression and activity of miSCA1; Access restricted to subscribers
UR  - https://hstalks.com/bs/2877/
UR  - https://hstalks.com/bs/p/37/
UR  - https://hstalks.com/bs/p/808/
ER  -