TY  - ADVS
AU  - High,Katherine A.
TI  - Gene therapy for Hemophilia
T2  - Gene transfer and gene therapy,
PY  - 2014///
CY  - London
PB  - Henry Stewart Talks
KW  - Gene therapy
KW  - Genetic transformation
KW  - Genetic vectors
KW  - Therapeutic use
KW  - Hemophilia
KW  - Viral genetics
KW  - Dependovirus
KW  - genetics
KW  - Gene Transfer Techniques
KW  - Genetic Therapy
KW  - methods
KW  - Genetic Vectors
KW  - therapeutic use
KW  - Hemophilia A
KW  - therapy
KW  - Hemophilia B
N1  - Animated audio-visual presentation with synchronized narration; Title from title frames; Contents: Hemophilia treatment past and present -- Gene transfer for genetic disease -- Viruses engineered to deliver genes -- Gene therapy using integrating vectors -- Adeno-associated virus (AAV) structure and composition -- AAV-Factor IX vectors -- AAV-mediated gene transfer for hemophilia -- Risk of germline transmission -- Peptide library based on AAV and Factor IX -- Transaminitis and liver enzymes -- Neutralizing antibodies to AAV -- Self-complementary DNA and Factor IX synthesis -- Strategies to overcome immunity to AAV -- Use of empty capsids; Access restricted to subscribers
UR  - https://hstalks.com/bs/2879/
UR  - https://hstalks.com/bs/p/808/
ER  -