TY  - ADVS
AU  - Mark,Brian
TI  - GM2 gangliosidosis future treatments: part 2 of 2 
T2  - Protein epidemiology : understanding human diseases at the level of protein structure and function,
PY  - 2017///
CY  - London
PB  - Henry Stewart Talks
KW  - Nervous system
KW  - Diseases
KW  - Tay-Sachs disease
KW  - G(M2) Ganglioside
KW  - Gangliosidoses, GM2
KW  - drug therapy
KW  - pathology
KW  - Hexosaminidase A
KW  - Hexosaminidases
KW  - Sandhoff Disease
KW  - Tay-Sachs Disease
N1  - Animated audio-visual presentation with synchronized narration; Title from title frames; Contents: Challenges of HexA delivery with AAV -- HexM modelling and interaction with GM2 -- GM2 clearance by AAV9-Hex vectors -- HexM delivery to Sandhoff disease mice; Access restricted to subscribers
UR  - https://hstalks.com/bs/3530/
UR  - https://hstalks.com/bs/p/33/
ER  -