Brunetti-Pierri, Nicola,
Helper-dependent adenoviral vectors for gene therapy [electronic resource] / Nicola Brunetti-Pierri. - London : Henry Stewart Talks, 2014. - 1 online resource (1 streaming video file (57 min.) : color, sound). - Gene transfer and gene therapy, 2056-452X . - Henry Stewart talks. Biomedical & life sciences collection. Gene transfer and gene therapy. .
Animated audio-visual presentation with synchronized narration. Title from title frames.
Contents: Overview of gene therapy vectors -- Helper-Dependent Ad (HDAd) vector -- Liver and lung directed gene therapy -- Hemophilia B gene therapy -- OTC deficiency clinical trial -- Balloon occlusion catheter-based delivery of HDAd -- HDAd-mediated CF gene therapy -- Brain gene therapy -- HDAd as genetic vaccine -- HDAd and stem cells.
Access restricted to subscribers.
Mode of access: World Wide Web.
3694 Henry Stewart Talks
Adenoviruses.
Gene therapy.
Genetic transformation.
Genetic vectors--Therapeutic use.
Liver--Diseases--Treatment.
Lungs--Diseases--Gene therapy.
Medical genetics.
Adenoviridae--genetics.
Brain Diseases--therapy.
Gene Transfer Techniques.
Genetic Therapy--methods.
Genetic Vectors--therapeutic use.
Helper Viruses--genetics.
Hemophilia B--therapy.
Liver Diseases--therapy.
Lung Diseases--therapy.
Ornithine Carbamoyltransferase Deficiency.
Helper-dependent adenoviral vectors for gene therapy [electronic resource] / Nicola Brunetti-Pierri. - London : Henry Stewart Talks, 2014. - 1 online resource (1 streaming video file (57 min.) : color, sound). - Gene transfer and gene therapy, 2056-452X . - Henry Stewart talks. Biomedical & life sciences collection. Gene transfer and gene therapy. .
Animated audio-visual presentation with synchronized narration. Title from title frames.
Contents: Overview of gene therapy vectors -- Helper-Dependent Ad (HDAd) vector -- Liver and lung directed gene therapy -- Hemophilia B gene therapy -- OTC deficiency clinical trial -- Balloon occlusion catheter-based delivery of HDAd -- HDAd-mediated CF gene therapy -- Brain gene therapy -- HDAd as genetic vaccine -- HDAd and stem cells.
Access restricted to subscribers.
Mode of access: World Wide Web.
3694 Henry Stewart Talks
Adenoviruses.
Gene therapy.
Genetic transformation.
Genetic vectors--Therapeutic use.
Liver--Diseases--Treatment.
Lungs--Diseases--Gene therapy.
Medical genetics.
Adenoviridae--genetics.
Brain Diseases--therapy.
Gene Transfer Techniques.
Genetic Therapy--methods.
Genetic Vectors--therapeutic use.
Helper Viruses--genetics.
Hemophilia B--therapy.
Liver Diseases--therapy.
Lung Diseases--therapy.
Ornithine Carbamoyltransferase Deficiency.